
- Deep knowledge in RNA biological mechanism to deliver RNA medicines with improved efficacy and PK/PD profile
- Biology insights to select promising and elusive targets of paramount fit for a diversified portfolio of RNA modalities
- Homegrown, exquisitely novel chemical modification to enable differentiated nucleic acid therapeutics
- Delivery platform established for liver and extrahepatic delivery across therapeutic area, i.e. CNS, ocular, oncology, etc
- Computational platform to optimize sequence design, chemical modification and delivery system
- Novel target identification from decoding phenotype to genotype via biomarker linkages